We are pleased to share the webinar organized by the IRDiRC member, Rare Diseases International (RDI) – “From Grassroots to Global: Growing Momentum towards the WHA Resolution on Rare Diseases”. […]
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Medicines Reimagined – The International Drug Repurposing Conference 2025 (#iDR25) hosted by REMEDi4ALL and Beacon aims to unlock the full potential of medicines by driving innovation for patient benefit. This global event […]
Read MoreWe are excited to announce the launch of several newly approved Task Forces and Working Groups focused on advancing the field of rare diseases. These groups bring together leading experts […]
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Fondazione Telethon announced that it has submitted the Marketing Authorization Application (MAA) for the gene therapy – etuvetidigene autotemcel – for the treatment of patients with Wiskott-Aldrich Syndrome (WAS), a rare genetic disease […]
Read MoreThe call for members for one Working Group and four new Task Forces is ongoing! The activities planned for 2025 are: (1) Task Force on “Preventive Medicines”: https://lnkd.in/eb4p-NSJPlease add in […]
Read MoreWe are pleased to share that the webinar series organized by Together for Rare Diseases & ERICA, brought together over 150+ members of the rare disease research community, who had […]
Read MoreWe are pleased to announce that the RE(ACT) Congress and IRDiRC Conference 2025 have extended the regular registration and abstract submission deadline until the end of January. Taking place from […]
Read MoreThe International Rare Diseases Research Consortium is launching a call for experts to support five new activities. Check out the newly approved Task Forces and Working Group : More details […]
Read MoreThe Interdisciplinary Scientific Committee (ISC) and Patient Advocacy Constituent Committee (PACC) are establishinga Task Force on “Stigma and rare diseases”. Globally more than 300 million people are living with a rare […]
Read MoreThe Therapies Scientific Committee (TSC) is establishinga Working Group on the Engagement of Young People Living with Rare Diseases in Therapy Development. The aim of the working group is to develop a landscape view […]
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